Latest News

Statistical Solutions Improve Accuracy of Clinical Trials with Rescue Therapy in Myasthenia Gravis

A new pilot study funded by the Myasthenia Gravis Rare Disease Network (MGNet) explores how statistical models can help improve clinical trials.

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Graph showing data simulation to illustrate the impact of rescue therapy on trial results.

CReATe Consortium initiates biomarker validation study in preparation for clinical trials

February 27, 2019

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Scientists at CCHMC Uncover Three Distinct Subtypes of Eosinophilic Esophagitis (EoE)

July 6, 2018

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Eosinophilic Esophagitis (EoE)

Investigating shared molecular targets between ANCA-associated vasculitis (AAV) and nephrotic syndrome (NS)

June 5, 2017

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spheres

mTOR pathway: a cross-consortium effort to understand mechanisms of rare diseases

June 4, 2017

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Selected Publications From RDCRN Consortia in 2015

January 1, 2016

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The First Gene for Primary Focal Dystonia

June 5, 2013

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Gene Mutation Responsible for SWS Identified

June 1, 2013

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The BVMC and Sturge-Weber Foundation logos appear over a gray graphic of molecules

Advocates Driving Research for a Cure – Scientific Meeting facilitates Communication, Collaboration and Progress

April 2, 2013

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