Latest News

Mapping the Natural History of Patients with Hereditary Spastic Paraplegia Type 4

Researchers from the Spastic Paraplegia Centers of Excellence Research Network (SP-CERN) have created the most detailed natural history of SPG4 to date.

Genotype-Structure-Phenotype Correlations Define Divergent Natural Histories in SPG4

Batten Disease Clinical Research Consortium Announces 2026 Early Career Investigator and Pilot Project Grant Awardees

May 7, 2026

Headshots of Dr. Chatzipli and Dr. Singh

Early Stage Investigator Spotlight: Andrew D. Tran, MD

April 15, 2026

Statistical Solutions Improve Accuracy of Clinical Trials with Rescue Therapy in Myasthenia Gravis

July 7, 2025

Graph showing data simulation to illustrate the impact of rescue therapy on trial results.

Pre-Doc Preparatory Program (P³) in Translational Research

June 23, 2025

MGNet Announces 2025 Scholars

December 9, 2024

Headshots of Dr. Sikorski and Dr. Wildberger

Former LDN Fellow Paves the Way for Earlier Diagnosis in Metachromatic Leukodystrophy

September 24, 2024

FCDGC Announces 2023 Pilot & Feasibility Project Awardee and Career Enhancement Fellow

April 11, 2023

A photo of Aryal Rajindra and Idris Wazeerud-din.

Training Program for Clinical Research in Rare Disease Launches New Session

November 9, 2022

Screenshot from a presentation on the Rare Diseases Research R25 Curriculum Grant