Latest News

Rare Research Report: October 2025

Each month, we share summaries of recent Rare Diseases Clinical Research Network grant-funded publications. Catch up on RDCRN research for October 2025.

Statistical Solutions Improve Accuracy of Clinical Trials with Rescue Therapy in Myasthenia Gravis

July 7, 2025

Graph showing data simulation to illustrate the impact of rescue therapy on trial results.

Pre-Doc Preparatory Program (P³) in Translational Research

June 23, 2025

MGNet Announces 2025 Scholars

December 9, 2024

Headshots of Dr. Sikorski and Dr. Wildberger

Former LDN Fellow Paves the Way for Earlier Diagnosis in Metachromatic Leukodystrophy

September 24, 2024

FCDGC Announces 2023 Pilot & Feasibility Project Awardee and Career Enhancement Fellow

April 11, 2023

A photo of Aryal Rajindra and Idris Wazeerud-din.

Training Program for Clinical Research in Rare Disease Launches New Session

November 9, 2022

Screenshot from a presentation on the Rare Diseases Research R25 Curriculum Grant

CPIC Announces 2022 Pilot Project Award Recipient

October 26, 2022

Early Stage Investigator Spotlight: Stephanie Sacharow Helps Patients with Phenylketonuria Overcome Barriers to Treatment

October 25, 2022