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Pompe Disease Over Time: What We’re Learning from a Natural History Study

To learn more about Pompe disease, the Lysosomal Disease Network (LDN) is conducting a natural history study, “Lysosomal Disease Network Longitudinal Study of Pompe Disease.”

Eosinophilic Gastrointestinal Diseases Over Time: What We’re Learning from a Natural History Study

July 22, 2024

Dystonia Over Time: What We’re Learning from a Natural History Study

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Phenylketonuria Over Time: What We’re Learning from a Natural History Study

May 28, 2024

Phelan-McDermid Syndrome Over Time: What We’re Learning from a Natural History Study

April 25, 2024

Primary Ciliary Dyskinesia Over Time: What We’re Learning from Natural History Studies

March 25, 2024

Severe Combined Immune Deficiency Over Time: What We’re Learning from Natural History Studies

December 12, 2023

Neonatal Enterovirus and Human Parechovirus Viral Sepsis Over Time: What We’re Learning from a Natural History Study

November 21, 2023

Urea Cycle Disorders Over Time: What We’re Learning from a Natural History Study

October 30, 2023