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Statistical Solutions Improve Accuracy of Clinical Trials with Rescue Therapy in Myasthenia Gravis

A new pilot study funded by the Myasthenia Gravis Rare Disease Network (MGNet) explores how statistical models can help improve clinical trials.

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Graph showing data simulation to illustrate the impact of rescue therapy on trial results.

Patient Advocate Spotlight: Kristen Hutchinson Spytek Accelerates Awareness and Research in Congenital Cytomegalovirus

October 18, 2022

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Patient Advocate Spotlight: Erica Barnes Fights for Children with Metachromatic Leukodystrophy and Other Rare Diseases

August 30, 2022

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Headshot of Erica Barnes, MS, CCC-SLP

Patient Advocate Spotlight: Kristin Anthony Brings Expertise in PTEN Hamartoma Tumor Syndrome Advocacy to New Role as Chair of RDCRN Patient Groups

August 5, 2022

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Headshot of Kristin Anthony

Patient Advocate Spotlight: Andrea Miller Creates Global Connections for Congenital Disorders of Glycosylation

July 7, 2022

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Andrea and her daughter, Bianca, celebrating World CDG Awareness Day

Patient Advocate Spotlight: Mark Rudolph Supports and Connects the Dystonia Community

May 17, 2022

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Headshot of Mark Rudolph

Patient Advocate Spotlight: Connie Lee Creates Connections for Cerebral Cavernous Malformation Research

October 26, 2021

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Connie-Lee

Patient Advocate Spotlight: Kristen Wheeden Steps into Lead Role for RDCRN Patient Groups

August 2, 2021

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Kristen Wheeden and her son, Brady, standing on their porch

Consortium Spotlight: New Consortium Targets Congenital and Perinatal Infections

January 26, 2021

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CPIC central unit
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