Latest News
Statistical Solutions Improve Accuracy of Clinical Trials with Rescue Therapy in Myasthenia Gravis
A new pilot study funded by the Myasthenia Gravis Rare Disease Network (MGNet) explores how statistical models can help improve clinical trials.
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Pompe Disease Over Time: What We’re Learning from a Natural History Study
September 25, 2024
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Former LDN Fellow Paves the Way for Earlier Diagnosis in Metachromatic Leukodystrophy
September 24, 2024
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