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Rare Research Report: December 2025
Each month, we share summaries of recent Rare Diseases Clinical Research Network grant-funded publications. Catch up on RDCRN research for December 2025.
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Pompe Disease Over Time: What We’re Learning from a Natural History Study
September 25, 2024
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Former LDN Fellow Paves the Way for Earlier Diagnosis in Metachromatic Leukodystrophy
September 24, 2024
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